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Human gene therapy, v.33 no.17/18, 2022년, pp.893 - 912
McLachlan, Gerry (The Roslin Institute & R(D)SVS, University of Edinburgh, Edinburgh, United Kingdom) , Alton, Eric W.F.W. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Boyd, A. Christopher (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Clarke, Nora K. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Davies, Jane C. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Gill, Deborah R. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Griesenbach, Uta (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Hickmott, Jack W. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Hyde, Stephen C. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Miah, Kamran M. (UK Respiratory Gene Therapy Consortium, London, United Kingdom) , Molina, Claudia Juarez (UK Respiratory Gene Therapy Consortium, London, United Kingdom)
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The prospect of gene therapy for inherited and acquired respiratory disease has energized the research community since the 1980s, with cystic fibrosis, as a monogenic disorder, driving early efforts to develop effective strategies. The fact that there are still no approved gene therapy products for ...
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